MPN Diagnostics
Bone marrow histology features of MPN
That can be assessed with reasonable consistency:
Overall haemopoietic cellularity
Relative predominance of increased megakaryocyte numbers
Megakaryocyte distribution (not the cytological details)
Reticulin pattern
Fibrosis Grade
WHO 0-3
Bain 1-4
Grade of fibrosis predicts overall survival
PT-1 Trial – 5 yr OS – Approx 95% for grade 0/1, Approx 87% for grade 3/4
Phenotypic ‘Driver’ Mutations
CML Molecular genetics
Depending on the breakpoints in the BCR and ABL1 genes, different sized proteins will be formed from the fusion gene:
e1a2 protein - p190 (seen in ALL > CML)
b2a2/b3a2 proteins - p210 (most common in CML)
e19a2 protein - p230
This is important diagnostically, and need to know which transcript is present when comes to quantitating its presence by RT-PCR. Different transcripts will need different primers for the lab test —> not all transcripts can be quantified in all labs.
JAK2 & MPL Mutations
Mutated JAK2/MPL is activated spontaneously without the presence of the usually required ligands —> persistent activation of the downstream pathways – e.g. STAT, PI3K, MAPK
JAK2 V617F at CUH Lab
Quantitative PCR using a fluorescent probe that is released as the allele replicates
One probe for the mutant allele and one for the wild type
Compare fluorescence of each to quantify
MPL and JAK2 Exon 12 at CUH
High resolution melt profile performed after PCR has produced the protein
Difference in the way mutated protein melts at 84 degrees
CALR Mutation
Insertion or deletions in Exon 9 are the most common mutations.
CALR is an endoplasmic protein, mutation leads to abnormal movement of MPL within the cell
CALR at CUH Lab
Primer for the area of interest within the CALR gene
The length of the protein produced during replication will tell you if mutated – shorter or longer than the wild type (deletions or insertions)
NGS Panels
Next generation sequencing to test whole panels of genes in a single assay
Sensitive for detecting mutations at low levels
Can test several patients within one assay —> reduces costs
Ion Torrent Analyser used at CUH
Currently for MF (not PV or ET)
Significance of results
Increasing no. of mutated genes detected in panel —> predicts high molecular risk disease
Future of testing
BCR/ABL, JAK2, CALR, MPL may put into a single panel and run all at once
May not be quite a sensitive as individual JAK2 assay ?significance of this
Personalised Risk Assessment in MPN
Available online from The Sanger Institute - here